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    MacroGenics, Inc.

    MacroGenics, Inc.

    MacroGenics is a clinical-stage biopharmaceutical company focused on discovering a...

    MacroGenics is a clinical-stage biopharmaceutic...

    uniQure N.V.

    uniQure N.V.

    uniQure is delivering on the promise of gene therapy -- single treatments with pot...

    uniQure is delivering on the promise of gene th...

    Astellas Pharma, Inc.

    Astellas Pharma, Inc.

    Astellas Pharma Inc. is a pharmaceutical company committed to the therapeutic fiel...

    Astellas Pharma Inc. is a pharmaceutical compan...

    Alder BioPharmaceuticals, Inc.

    Alder BioPharmaceuticals, Inc.

    Alder BioPharmaceuticals is a clinical-stage biopharmaceutical company focused on ...

    Alder BioPharmaceuticals is a clinical-stage bi...

    Kiniksa Pharmaceuticals, Ltd.

    Kiniksa Pharmaceuticals, Ltd.

    We are a biopharmaceutical company focused on discovering, acquiring, developing a...

    We are a biopharmaceutical company focused on d...

    Ultragenyx Pharmaceutical Inc.

    Ultragenyx Pharmaceutical Inc.

    Ultragenyx is a biopharmaceutical company committed to bringing to patients novel ...

    Ultragenyx is a biopharmaceutical company commi...

    Insmed, Inc.

    Insmed, Inc.

    At Insmed we are on a mission to transform the lives of patients battling serious ...

    At Insmed we are on a mission to transform the ...

    Capricor Therapeutics, Inc.

    Capricor Therapeutics, Inc.

    Capricor Therapeutics, Inc. (Nasdaq: CAPR) is a clinical-stage biotechnology compa...

    Capricor Therapeutics, Inc. (Nasdaq: CAPR) is a...

    BioMarin Pharmaceutical Inc.

    BioMarin Pharmaceutical Inc.

    At BioMarin, we focus on developing first-in-class and best-in-class therapeutics ...

    At BioMarin, we focus on developing first-in-cl...